Partnerships in Developing New JM Treatments

In October, Cure JM had two speakers give an update about drug discovery in juvenile myositis. Joni L. Rutter, Ph.D., Director, National Center for Advancing Translational Sciences, National Institutes of Health, updated families about the process of drug discovery and development and how partnerships like Cure JM’s NCATS partnership accelerate new treatments for juvenile myositis. Eric Hoffman, Ph.D., President and CEO, of ReveraGen Pharmaceutical, brought families into the inner circle of understanding how new drugs move through the process and the role that Cure JM, parents, patients, and grandparents play in this process.

Click the link above to watch the informative presentation.

Affordable and Accessible Treatments for JM

Affordable and Accessible Treatments for JM

Two special guest speakers, Michelle Vogel, MPA, IV Solutions RX, and Laurel Cherwin, BSN, RN, IgCN, Octapharma, shared information on navigating affordable treatments and care for JM patients.

The FDA’s Ruling on Vamorolone in DMD

You may have heard about yesterday’s FDA ruling, which approved vamorolone as an alternative steroid for use in Duchenne muscular dystrophy.

Vamorolone is a new steroid alternative with fewer side effects than prednisone. The drug aims to preserve the beneficial anti-inflammatory and muscle-strengthening characteristics of corticosteroids, while decreasing some of the unwelcome side effects, including bone fragility, delayed growth, and behavior changes.

As we learned in yesterday’s announcement, vamorolone was found to be both safe and effective as a therapy for Duchenne muscular dystrophy in its newly approved indication.

Ways to help your kids and yourself cope living with JM

Cure JM Mental Health Coordinator, Suzanne Edison discusses ways to help your kids and yourself cope living with JM. Learn about emotional and behavioral challenges that often come with chronic diseases like juvenile myositis and ways to help patients and caregivers cope.

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